Published online Sep 26, 2020. doi: 10.12998/wjcc.v8.i18.4252
Peer-review started: February 25, 2020
First decision: July 4, 2020
Revised: July 18, 2020
Accepted: August 14, 2020
Article in press: August 14, 2020
Published online: September 26, 2020
Processing time: 209 Days and 12.1 Hours
Gitelman syndrome (GS) is an unusual, autosomal recessive salt-losing tubulopathy characterized by hypokalemic metabolic alkalosis, hypomagnesemia and hypocalciuria. It is caused by mutations in the solute carrier family 12 member 3 (SLC12A3) gene resulting in disordered function of the thiazide-sensitive NaCl co-transporter. To date, many types of mutations in the SLC12A3 gene have been discovered that trigger different clinical manifestations. Therefore, gene sequencing should be considered before determining the course of treatment for GS patients.
A 55-year-old man was admitted to our department due to hand numbness and fatigue. Laboratory tests after admission showed hypokalemia, metabolic alkalosis and renal failure, all of which suggested a diagnosis of GS. Genome sequencing of DNA extracted from the patient’s peripheral blood showed a rare homozygous mutation in the SLC12A3 gene (NM_000339.2: chr16:56903671, Exon4, c.536T>A, p.Val179Asp). This study reports a rare homozygous mutation in SLC12A3 gene of a Chinese patient with GS.
Genetic studies may improve the diagnostic accuracy of Gitelman syndrome and improve genetic counseling for individuals and their families with these types of genetic disorders
Core Tip: In this manuscript, we report a patient with severe hypokalemia who was diagnosed with Gitelman syndrome by genome sequencing. We found a relatively unusual homozygous mutation in the SLC12A3 gene, which has been rarely reported previously. This patient also had elevated creatinine, different to the general Gitelman syndrome, suggesting that some factors, including this type of mutation, may cause renal impairment.