Published online Jul 16, 2025. doi: 10.12998/wjcc.v13.i20.102651
Revised: January 21, 2025
Accepted: March 4, 2025
Published online: July 16, 2025
Processing time: 166 Days and 22.8 Hours
Floating-harbor syndrome (FHS) is a rare genetic disorder caused by pathogenic variants in the SRCAP gene. Most individuals with FHS have short stature, delayed speech and language development, and dysmorphic facial features. However, the patients with FHS are not easy to diagnose due to the overlap of clinical phenotypes with other disorders.
We reported a 10-year-old boy who presented with severe short stature, developmental delay and distinctive facial features. Exome sequencing was provided for the proband and his parents. We identified a novel frameshift variant c.7235de
This case confirms that the c.7235delinsGT (p.Thr2412fs) variant in the SRCAP gene is associated with FHS and expands the spectrum of SRCAP variants.
Core Tip: In conclusion, a de novo heterozygous variant in SRCAP (c.7235delinsGT; p.Thr2412fs) was identified in a Chinese male patient with floating-harbor syndrome (FHS) using ES. This proband exhibited classical clinical features of FHS, including severe short stature, developmental delay, characteristic facial features, and additional malformations. This novel SRCAP variant expands the known variant spectrum in FHS and supports the clinical homogeneity of this disorder. Fortunately, we provided genetic counseling and prenatal genetic diagnosis for this family based on the known variant in the proband.