Basic Study
Copyright ©The Author(s) 2022. Published by Baishideng Publishing Group Inc. All rights reserved.
World J Clin Oncol. May 24, 2022; 13(5): 323-338
Published online May 24, 2022. doi: 10.5306/wjco.v13.i5.323
Tumor specifically internalizing peptide ‘HN-1’: Targeting the putative receptor retinoblastoma-regulated discoidin domain receptor 1 involved in metastasis
Frank-Un Hong, Miguel Castro, Klaus Linse
Frank-Un Hong, Miguel Castro, Klaus Linse, Research & Development, Bio-Synthesis, Inc., Lewisville, TX 75057, United States
Author contributions: Hong FU has worked on cancer genetics and molecular pharmacology; Castro M participated in therapeutics research; Linse K performed molecular modeling to predict the structure of peptides; Hong FU, Castro M, and Linse K meet the criteria for authorship established by the International Committee of Medical Journal Editors and verify the validity of the results reported; Hong FU wrote the manuscript; all authors approved the final version of the article.
Conflict-of-interest statement: Dr. Hong has received royalties from University of Texas M. D. Anderson Cancer Center patent covering materials related to HN-1 peptide. All other authors have nothing to disclose.
Data sharing statement: No additional data available.
Open-Access: This article is an open-access article that was selected by an in-house editor and fully peer-reviewed by external reviewers. It is distributed in accordance with the Creative Commons Attribution NonCommercial (CC BY-NC 4.0) license, which permits others to distribute, remix, adapt, build upon this work non-commercially, and license their derivative works on different terms, provided the original work is properly cited and the use is non-commercial. See: https://creativecommons.org/Licenses/by-nc/4.0/
Corresponding author: Frank-Un Hong, PhD, Research Scientist, Research & Development, Bio-Synthesis, Inc., 612 E Main St, Lewisville, TX 75057, United States. frank_hong@biosyn.com
Received: April 9, 2021
Peer-review started: April 9, 2021
First decision: June 28, 2021
Revised: July 6, 2021
Accepted: April 22, 2022
Article in press: April 22, 2022
Published online: May 24, 2022
Processing time: 410 Days and 11.2 Hours
Abstract
BACKGROUND

Less than 0.5% of intravenously injected drugs reach tumors, contributing to side effects. To limit damage to healthy cells, various delivery vectors have been formulated; yet, previously developed vectors suffer from poor penetration into solid tumors. This issue was resolved by the discovery of HN-1 peptide isolated via biopanning a phage-display library. HN-1 targets human head and neck squamous cell carcinoma (HNSCC) (breast, thyroid; potentially lung, cervix, uterine, colon cancer), translocates across the cell membrane, and efficiently infiltrates solid tumors. HN-1 peptide has been conjugated to various anticancer drugs and imaging agents though the identity of its receptor remained enigmatic.

AIM

To decipher the clues that pointed to retinoblastoma (Rb)-regulated discoidin-domain receptor 1 as the putative receptor for HN-1 is described.

METHODS

HN-1 peptide was synthesized and purified using reverse-phase high-performance liquid chromatography and gel electrophoresis. The predicted mass was confirmed by mass spectroscopy. To image the 3-dimensional structure of HN-1 peptide, PyMOL was used. Molecular modeling was also performed with PEP-FOLD3 software via RPBS bioinformatics web portal (INSERM, France). The immunohistochemistry results of discoidin domain receptor 1 (DDR1) protein were obtained from the publicly accessible database in the Human Protein Atlas portal, which contained the images of immunohistochemically labeled human cancers and the corresponding normal tissues.

RESULTS

The clues that led to DDR1 involved in metastasis as the putative receptor mediating HN-1 endocytosis are the following: (1) HN-1 is internalized in phosphate-buffered saline and its uptake is competitively inhibited; (2) HN-1 (TSPLNIHNGQKL) exhibits similarity with a stretch of amino acids in alpha5 beta3 integrin (KLLITIHDRKEF). Aside from two identical residues (Ile-His) in the middle, the overall distribution of polar and nonpolar residues throughout the sequences is nearly identical. As HN-1 sequence lacks the Arg-Gly-Asp motif recognized by integrins, HN-1 may interact with an "integrin-like" molecule. The tertiary structure of both peptides showed similarity at the 3-dimensional level; (3) HN-1 is internalized by attached cells but not by suspended cells. As culture plates are typically coated with collagen, collagen-binding receptor (expressed by adherent but not suspended cells) may represent the receptor for HN-1; (4) DDR1 is highly expressed in head and neck cancer (or breast cancer) targeted by HN-1; (5) Upon activation by collagen, DDR1 becomes internalized and compartmentalized in endosomes consistent with the determination of ’energy-dependent clathrin-mediated endocytosis’ as the HN-1 entry route and the identification of HN-1 entrapped vesicles as endosomes; and (6) DDR1 is essential for the development of mammary glands consistent with the common embryonic lineage rationale used to identify breast cancer as an additional target of HN-1. In summary, collagen-activated tyrosine kinase receptor DDR1 overexpressed in HNSCC assumes a critical role in metastasis. Further studies are warranted to assess HN-1 peptide’s interaction with DDR1 and the therapeutic potential of treating metastatic cancer. Additionally, advances in delivery (conformation, endocytic mechanism, repertoire of targeted cancers of HN-1 peptide), tracking (HN-1 conjugated imaging agents), and activity (HN-1 conjugated therapeutic agents) are described.

CONCLUSION

The discovery of DDR1 as HN-1 peptide’s putative receptor represents a significant advance as it enables identification of metastatic cancers or clinical application of previously developed therapeutics to block metastasis.

Keywords: HN-1 peptide; Solid tumor; Targeted drug delivery; Discoidin domain receptor 1; Tyrosine kinase; Metastasis

Core Tip: The side effects associated with current drugs are exacerbated by the accumulation of administered drugs in non-tumor tissues. To guide, various tumor-homing vectors have been developed though their delivery efficacy is limited by poor penetration into solid tumors. To resolve, the ‘tumor specifically internalizing peptide’ HN-1 was isolated via biopanning a phage-display library. HN-1 peptide targets human head and neck squamous cell carcinoma (breast, thyroid, potentially cervical, lung, uterine, colon cancer), translocates across the cell membrane and effectively penetrates solid tumors. Here, deciphering of the clues that pointed to discoidin domain receptor 1 as the putative receptor for HN-1 is described.