Published online Mar 9, 2025. doi: 10.5409/wjcp.v14.i1.96643
Revised: October 3, 2024
Accepted: December 6, 2024
Published online: March 9, 2025
Processing time: 222 Days and 12.8 Hours
Cellular therapies have started an important new therapeutic direction in autistic spectrum disorder (ASD), and the ample diversity of ASD pathophysiology and the different types of cell therapies prompt an equally ample effort to employ clinical studies for studying the ASD causes and cell therapies. Stem cells have yielded so far mixed results in clinical trials, and at patient level the results varied from impressive to no improvement. In this context we have administered autologous cord blood (ACB) and a non-placebo, material intervention repre
To compare the efficacy of ACB vs ICS and find markers correlated with the child's progress in order to better predict ACB efficacy.
CORDUS clinical study is a crossover study in which both oral ICS and intravenous ACB were sequentially administered to 56 children; ACB was infused as an inpatient procedure. Treatment efficacy was evaluated pre-treatment and post-treatment at 6 months by an independent psychotherapist with Autism Treatment Evaluation Checklist, Quantitative Checklist for Autism in Toddlers and a 16-item comparative table score, after interviewing the children’s parents and therapists. Before and after each intervention participants had a set of blood tests including inflammatory, metabolic and oxidative markers, and the neuronal specific enolase.
No serious adverse reactions were noted during and after cord blood or supplement administration. ACB improved evaluation scores in 78% of children with age 3–7-years (n = 28), but was much less effective in kids older than 8 years or with body weight of more than 35 kg (n = 28; only 11% of children improved scores). ICS yielded better results than ACB in 5 cases out of 28, while in 23 kids ACB brought more improvement than ICS (P < 0.05); high initial levels of inflammation and ferritin were associated with no improvement. Ample individual differences were noted in children's progress, and statistically significant improvements were seen after ACB on areas such as verbalization and social interaction, but not on irritability or aggressive behavior.
ACB has superior efficacy to ICS in ASD; high inflammation, ferritin, age and body weight predict less improvement; more clinical studies are needed for studying ACB efficacy in ASD.
Core Tip: CORDUS clinical study aimed to find factors correlated to therapeutic efficacy in autistic spectrum disorder (ASD) by comparing sequential administration of autologous cord blood (ACB) and individualised supplements and testing both the ASD children and the ACB. High initial levels of inflammation markers (erythrocyte sedimentation rate, C-reactive protein, tumor necrosis factor-alpha, α-2 globulins) or ferritin, but not high initial levels of neuronal specific enolase (NSE), were correlated with little or no improvement after cord blood administration. In some patients NSE was lowered after ACB. In a few patients improvement on specific supplements was superior to cord blood. Further studies are needed for finding predictors of cord blood efficacy in ASD.