Original Article
Copyright ©2010 Baishideng. All rights reserved.
World J Gastroenterol. May 7, 2010; 16(17): 2100-2108
Published online May 7, 2010. doi: 10.3748/wjg.v16.i17.2100
Inhibition of hepatitis C virus replication by single-stranded RNA structural mimics
Robert Smolic, Martina Smolic, John H Andorfer, Catherine H Wu, Robert M Smith, George Y Wu
Robert Smolic, Martina Smolic, John H Andorfer, Catherine H Wu, Robert M Smith, George Y Wu, Department of Medicine, Division of Gastroenterology-Hepatology, University of Connecticut Health Center, 263 Farmington Ave., Farmington, CT 06030-1845, United States
Author contributions: Smolic R, Smolic M, Andorfer JH, Wu CH, Smith RM and Wu GY contributed equally to this work; Smolic R, Smith RM and Wu GY designed the research; Smolic R, Smolic M, Smith RM and Andorfer JH performed the research; Wu CH contributed new reagents/analytic tools; Smolic R, Smolic M and Wu GY wrote the paper.
Supported by In part Grants from NIDDK DK042182 and the Herman Lopata Chair for Hepatitis Research (Wu GY)
Correspondence to: George Y Wu, MD, PhD, Department of Medicine, Division of Gastroenterology-Hepatology, University of Connecticut Health Center, 263 Farmington Ave., Farmington, CT 06030-1845, United States. wu@nso.uchc.edu
Telephone: +1-860-6792509 Fax: +1-860-6793159
Received: August 12, 2009
Revised: November 13, 2009
Accepted: November 20, 2009
Published online: May 7, 2010
Abstract

AIM: To examine the effect of hepatitis C virus (HCV) structural mimics of regulatory regions of the genome on HCV replication.

METHODS: HCV RNA structural mimics were constructed and tested in a HCV genotype 1b aBB7 replicon, and a Japanese fulminant hepatitis-1 (JFH-1) HCV genotype 2a infection model. All sequences were computer-predicted to adopt stem-loop structures identical to the corresponding elements in full-length viral RNA. Huh7.5 cells bearing the BB7 replicon or infected with JFH-1 virus were transfected with expression vectors generating HCV mimics and controls. Cellular HCV RNA and protein levels were quantified by real-time polymerase chain reaction and Western blotting, respectively. To evaluate possible antisense effects, complementary RNAs spanning a mimic were prepared.

RESULTS: In the BB7 genotype 1b replicon system, mimics of the polymerase (NS-5B), X and BA regions inhibited replication by more than 90%, 50%, and 60%, respectively. In the JFH-1 genotype 2 infection system, mimics that were only 74% and 46% identical in sequence relative to the corresponding region in JFH-1 inhibited HCV replication by 91.5% and 91.2%, respectively, as effectively as a mimic with complete identity to HCV genotype 2a. The inhibitory effects were confirmed by NS3 protein levels. Antisense RNA molecules spanning the 74% identical mimic had no significant effects.

CONCLUSION: HCV RNA structural mimics can inhibit HCV RNA replication in replicon and infectious HCV systems and do so independent of close sequence identity with the target.

Keywords: Hepatitis C virus; Japanese fulminant hepatitis virus; Complementarity; RNA sequence; Hybridization