For: | Junge N, Yuan Q, Vu TH, Krooss S, Bednarski C, Balakrishnan A, Cathomen T, Manns MP, Baumann U, Sharma AD, Ott M. Homologous recombination mediates stable Fah gene integration and phenotypic correction in tyrosinaemia mouse-model. World J Hepatol 2018; 10(2): 277-286 [PMID: 29527263 DOI: 10.4254/wjh.v10.i2.277] |
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URL: | https://www.wjgnet.com/1948-5182/full/v10/i2/277.htm |
Number | Citing Articles |
1 |
Laura Torella, Nerea Santana‐Gonzalez, Nerea Zabaleta, Gloria Gonzalez Aseguinolaza. Gene editing in liver diseases. FEBS Letters 2024; doi: 10.1002/1873-3468.14989
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2 |
Samantha L. Ginn, Sharntie Christina, Ian E. Alexander. Curing Genetic Diseases Through Genome Reprogramming. Progress in Molecular Biology and Translational Science 2021; 182: 257 doi: 10.1016/bs.pmbts.2021.01.030
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3 |
Cintia J. Monteiro, David M. Heery, Jonathan B. Whitchurch. Genome Editing in Biomedical Sciences. Advances in Experimental Medicine and Biology 2023; 1429: 13 doi: 10.1007/978-3-031-33325-5_2
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4 |
Maximiliano L. Cacicedo, Christine Weinl-Tenbruck, Daniel Frank, Sebastian Wirsching, Beate K. Straub, Jana Hauke, Jürgen G. Okun, Nigel Horscroft, Julia B. Hennermann, Fred Zepp, Frédéric Chevessier-Tünnesen, Stephan Gehring. mRNA-based therapy proves superior to the standard of care for treating hereditary tyrosinemia 1 in a mouse model. Molecular Therapy - Methods & Clinical Development 2022; 26: 294 doi: 10.1016/j.omtm.2022.07.006
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5 |
Federico Mingozzi, Norman Junge. Pediatric Liver Transplantation. 2021; : 320 doi: 10.1016/B978-0-323-63671-1.00033-1
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6 |
Pasquale Piccolo, Alessandro Rossi, Nicola Brunetti-Pierri. Liver-directed gene-based therapies for inborn errors of metabolism. Expert Opinion on Biological Therapy 2021; 21(2): 229 doi: 10.1080/14712598.2020.1817375
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7 |
Madhumita Premkumar, Virendra Singh. Biomedical Translational Research. 2022; : 273 doi: 10.1007/978-981-16-8845-4_14
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8 |
Marcel A. Chuecos, William R. Lagor. Liver directed adeno‐associated viral vectors to treat metabolic disease. Journal of Inherited Metabolic Disease 2024; 47(1): 22 doi: 10.1002/jimd.12637
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9 |
Giulia Bortolussi, Alessandra Iaconcig, Giulia Canarutto, Fabiola Porro, Filippo Ferrucci, Claudia Galletta, Cristian Díaz-Muñoz, Vipin Rawat, Alessia De Caneva, Olayemi Joseph Olajide, Lorena Zentilin, Silvano Piazza, Luka Bočkor, Andrés Fernando Muro. CRISPR-Cas9-mediated somatic correction of a one-base deletion in the Ugt1a gene ameliorates hyperbilirubinemia in Crigler-Najjar syndrome mice. Molecular Therapy - Methods & Clinical Development 2023; 31: 101161 doi: 10.1016/j.omtm.2023.101161
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10 |
Simon Alexander Krooss, Zhen Dai, Florian Schmidt, Alice Rovai, Julia Fakhiri, Akshay Dhingra, Qinggong Yuan, Taihua Yang, Asha Balakrishnan, Lars Steinbrück, Sangar Srivaratharajan, Michael Peter Manns, Axel Schambach, Dirk Grimm, Jens Bohne, Amar Deep Sharma, Hildegard Büning, Michael Ott. Ex Vivo/In vivo Gene Editing in Hepatocytes Using “All-in-One” CRISPR-Adeno-Associated Virus Vectors with a Self-Linearizing Repair Template. iScience 2020; 23(1): 100764 doi: 10.1016/j.isci.2019.100764
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